Keeping Up with Rare Disease Therapies: Pipeline to Management Solutions Track

ACPE UAN #:  0233-0000-20-021-H04-P

Release Date:  October 22, 2020

Expiration Date:   October 22, 2023

Activity Type:    Knowledge-based

Contact Hours:   1

Activity Fee:  Member:  $15        Non-Member:  $30

Target Audience: Pharmacists who practice in managed care settings.

Activity Description

Over the last several years, payers have increased their focus on the management of rare diseases. When compared to 2008, the number of agents granted orphan drug designation has more than tripled in 2020. While these agents represent scientific breakthroughs and significant medical progress, the cost of these treatments may also require close monitoring of the pipeline, assessment of potential budget impact and appropriate managed care strategies to ensure safe and appropriate use in patients.

This session will provide a current landscape of rare disease management and a summary of new treatments likely to be available for rare diseases. In addition, this session will demonstrate the role of clinical programs to manage the utilization of rare disease treatments and explore proposed models to manage the costs related to rare disease therapies

Learning Objectives:

At the completion of this activity, participants should be able to:

  1.  Summarize the current landscape and anticipated future trends with rare disease therapies.
  2.  Identify at least three treatment options for rare disease currently in the pipeline and the potential   impact on the specific disease.
  3.  Identify at least two challenges payers face when managing rare diseases.
  4.  Discuss at least two management opportunities and their potential impact on patient outcomes and spend.

Schedule of Educational Activity:

This activity consists of an audio recording, pre-test assessment questions (not required to pass to continue), post-test questions (required to pass with a score of 70% or higher), and a specific activity evaluation.

Accreditation Statement:

The Academy of Managed Care Pharmacy (AMCP) is accredited by the Accreditation Council for Pharmacy Education as a provider of continuing pharmacy education

As an accredited provider, AMCP strictly adheres to the ACPE Standards for Commercial Support and other relevant guidelines and standards to ensure the independence of continuing pharmacy education (CPE) activities.  AMCP intends that all CPE activities be independent, objective, balanced, evidence-based, and free of any commercial bias.

CPE Requirements:   

Participants should claim CPE credit for this home study activity only if they have not claimed credit for the live activity presented at AMCP Nexus 2020 Virtual.


CPE credit will be processed through the AMCP Learn portal and reported directly to CPE Monitor.  Please allow 72 hours for processing and posting in your National Association of Boards of Pharmacy (NABP) e-Profile account.

To receive credit for a home study activity you must:

  •  Review the full content of the home study activity.
  •  Complete the post-test and achieve a score of 70% or higher.
  •  Complete a specific activity evaluation.

System Technical Requirements/Viewing Requirements

Courses and continuing education activities are delivered via your Web browser and Acrobat PDF.  For all activities, you should have a basic comfort level using a computer and navigating websites. View the minimum technical and system requirements for all continuing education activities.

Credit Information

Activity Number Credit Amount Accreditation Period
ACPE UAN #0233-0000-20-021-H04-P 1 Contact Hour October 22, 2020 - October 22, 2023