Rare Disease Spotlight: Hemophilia Treatment Advances on the Horizon

Pricing: Free for Members and Non-Members

This activity is supported by an educational grant from BioMarin Pharmaceutical Inc.


Course Description

Diagnosis of rare diseases affecting the blood are increasing in incidence due to sophistication in diagnostics and molecular genetic discoveries and are particularly concerning because of the life-threatening complications. Hemophilia describes a duo of genetically inherited rare blood disorders, hemophilia A and hemophilia B, which lead to excessive bleeding episodes in sufferers. New FDA approved treatment options are expected within the next year, introducing novel mechanisms of action, gene-directed therapies, or alternate administration options to reduce treatment gaps and address unmet needs, also bringing complex managed care considerations to access to care and coverage design for single-investment durable cures.

During this session, faculty will focus on hemophilia treatment advances, identify considerations for developing payment models, and discuss innovative methods to address access to care.

Target Audience

Pharmacists who practice in managed care settings.

Learning Objectives

At the completion of this activity, participants should be able to:

  1. Review the incidence, current treatment options, and pipeline for hemophilia, a rare blood disorder.
  2. Identify managed care considerations for developing payment models for hemophilia.
  3. Discuss innovative methods to address access to care for the rare blood disease hemophilia and durable cure treatments in the pipeline.

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Rare Disease Spotlight: Hemophilia Treatment Advances

Pricing: Free for Members and Non-Members
Course summary
Available credit: 
  • 1.25 ACPE
    ACPE The Academy of Managed Care Pharmacy is accredited by the Accreditation Council for Pharmacy Education as a provider of continuing pharmacy education.
  • 1.25 Certificate of Completion
Course opens: 
05/14/2023
Course expires: 
01/31/2024
Cost:
$0.00

Faculty

Anne Jackson, FSA, MAAA
Principal and Consulting Actuary
Milliman, Inc.
Indianapolis, IN

Steven W. Pipe, MD
Professor of Pediatrics and Pathology
University of Michigan
Ann Arbor, MI

Moderator

James Gartner, BS, MBA
President
PerformRx
Pittsburgh, PA

Financial Relationship Disclosures

Faculty/Reviewer/PlannerReported Relevant Financial Relationships
Anne Jackson
Faculty		Disclosed no relevant financial relationships.
Steven Pipe
Faculty		Consultant: Apcintex, ASC Therapeutics, Bayer, BioMarin, CSL Behring, GeneVentiv, HEMA Biologics, Freeline Therapeutics, LFB, Novo Nordisk, Pfizer, Regeneron/Intellia, Roche/Genentech, Sangamo Therapeutics, Sanofi, Takeda, Spark Therapeutics, UniQure​

Julie Howard
Reviewer

Disclosed no relevant financial relationships.
Jennifer Evans
Planner		Disclosed no relevant financial relationships.
  • AMCP Staff have disclosed no relevant financial relationships.
  • If applicable, relevant financial relationships have been mitigated and documented.
  • Content has undergone a peer review to ensure content validity.

Accreditation:

The Academy of Managed Care Pharmacy (AMCP) is accredited by the Accreditation Council for Pharmacy Education as a provider of continuing pharmacy education.

ACPE UAN:0233-0000-22-043-H01-P • Activity Type: Knowledge-Based
Contact Hours: 1.25
Release Date: October 13, 2022 •  Expiration Date: December 31, 2023
Activity Fee: Free for Members and Non-Members

Participants should claim continuing pharmacy education (CPE) credit for this home study activity only if they have not claimed credit for the live activity presented at Nexus 2022. CPE credit will be processed through the AMCP Learn portal and reported directly to CPE Monitor. Please allow 72 hours for processing and posting in your NABP account.

To receive credit for an online activity you must:

  • Review the full content of the activity.
  • Successfully complete the post-test (required to pass with a score of 70% or higher, it may be taken a maximum of three times).
  • Complete a specific activity evaluation.
     

System Technical Requirements/Viewing Requirements:

System Requirements Courses and learning activities are delivered via your Web browser and Acrobat PDF. For all activities, you should have a basic comfort level using a computer and navigating websites. View the minimum technical and system requirements for continuing education online learning activities

Available Credit

  • 1.25 ACPE
    ACPE The Academy of Managed Care Pharmacy is accredited by the Accreditation Council for Pharmacy Education as a provider of continuing pharmacy education.
  • 1.25 Certificate of Completion

Price

Cost:
$0.00
Please login or register to take this course.

Required Hardware/software

System Requirements Courses and learning activities are delivered via your Web browser and Acrobat PDF. For all activities, you should have a basic comfort level using a computer and navigating websites. View the minimum technical and system requirements for continuing education online learning activities